-
2024-510742-13-00
5
2023-04-19
Pediatric low-grade glioma harboring an activating RAF alteration requ
-
2023-503444-13-00
5
2023-03-29
Relapsed/refractory multiple myeloma
-
2023-507052-69-00
4
2023-03-29
Multifocal Motor Neuropathy
-
2024-512890-28-00
5
2023-03-20
Primary immune thrombocytopenia (ITP)
-
2023-509583-22-00
4
2023-03-14
Neoplasms, Rectal
-
2022-501534-33-00
6
2023-03-06
Unexplained Subfertility, infertility
-
2024-512785-33-00
10
2023-03-01
Active Idiopathic Inflammatory Myopathy (IIM)
-
2024-514173-22-00
5
2023-02-28
Cystic Fibrosis
-
2024-511852-42-00
5
2023-01-19
Spinal Muscular Atrophy
-
2024-511707-42-00
5
2023-01-05
Spinal Muscular Atrophy
-
2023-505057-40-00
4
2022-12-02
Lung Cancer, Non-Small Cell
-
2023-504741-32-00
4
2022-11-30
Moderately to Severely Active Crohn's Disease
-
2023-504743-13-00
4
2022-11-30
Moderately to Severely Active Ulcerative Colitis
-
2024-515637-14-00
5
2022-11-08
Cystic Fibrosis
-
2024-514082-19-00
4
2022-11-04
Amyotrophic Lateral Sclerosis
-
2023-505067-36-00
1
2022-06-22
Advanced or Metastatic Solid Tumors
-
2024-513759-34-00
7
2022-05-31
Relapsed or Refractory Acute Leukemias
-
2023-507795-51-00
5
2022-05-17
atherosclerotic heart and blood vessel disease (the narrowing of arter
-
2023-504360-42-00
6
2022-05-13
Non-ST-segment elevation acute coronary syndrome
-
2024-514711-99-00
10
2022-05-02
FIGO stage III high grade serous ovarian cancer, peritoneal cancer, or
-
2023-507069-25-00
4
2022-04-29
Amyloid Light Chain Amyloidosis
-
2023-506486-60-01
5
2022-04-26
Heart transplant
-
2023-510054-16-00
4
2022-04-26
Primary Sjogren's syndrome
-
2024-512745-16-00
5
2022-04-13
Non–Transfusion-Dependent Alpha- or Beta-Thalassemia