Adeno-Associated Virus Serotype Rh79 Containing The Human Otc Gene

2 trials Orphan designation

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2 Registered trials

0 Recruiting

1 Completed trials

1 Sponsors

2 Countries

Phase I (FiH)

Phase I (FiH): 2

Oversight events:

3 temporary halts across 1 trial

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Sponsors using this IMP

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2 total

Long-term Follow-up (LTFU) Study of Participants in any iECURE Protocol Using an Investigational Product (IP) Pending

2024-514190-21-00 Phase I (FiH) 2 countries Iecure Inc.
An open-label study to investigate ECUR-506 in male children less than 9 months of age with neonatal onset OTC deficiency Ended

2023-506180-34-01 Phase I (FiH) 1 country Iecure Inc.

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