-
2025-522051-26-00
5
2026-04-23
Acquired Angioedema due to C1 Inhibitor Deficiency
-
2025-522512-16-00
3
2026-04-23
Metastatic Castration Resistant Prostate Cancer (mCRPC)
-
2024-518615-19-00
5
2026-04-22
Major Depressive Disorder
-
2024-517943-29-00
5
2026-04-21
Pulmonary Hypertension associated with interstitial lung disease (WHO
-
2025-522878-36-00
5
2026-04-20
Chronic Spontaneous Urticaria
-
2025-523234-66-00
4
2026-04-17
Well-Controlled Recurrent Pericarditis
-
2024-514006-31-00
9
2026-04-16
Non-active Progressive Multiple Sclerosis (PMS)
-
2025-521327-67-00
4
2026-04-13
Metastatic Castration-Resistant Prostate Cancer
-
2025-522145-21-00
5
2026-04-13
Metastatic hormone sensitive prostate cancer
-
2024-519818-31-01
5
2026-04-10
Endometrial Cancer
Advanced, Recurrent, Metastatic, or Primary Unresec
-
2025-521792-31-01
5
2026-04-07
Homozygous Familial Hypercholesterolemia (HoFH)
-
2025-522191-86-00
5
2026-04-02
Focal segmental glomerulosclerosis
-
2025-522279-27-00
5
2026-04-02
Newly Diagnosed AML with an NPM1 mutation
-
2025-521966-91-00
4
2026-03-31
Refractory Metastatic Breast Cancer with Liver Dominant Disease
-
2024-512436-29-00
11
2026-03-27
CARDIOVASCULAR DISEASES
-
2025-521142-22-00
5
2026-03-27
Hereditary Angioedema
-
2025-523204-68-00
4
2026-03-25
HER2-positive breast cancer
-
2025-522892-27-00
4
2026-03-21
Bronchiectasis
-
2025-521314-25-00
5
2026-03-19
NPM1-m and KMT2A-r Acute Myeloid Leukemia
-
2025-521884-12-00
5
2026-03-19
First line triple-negative breast cancer (TNBC)
-
2024-519555-28-00
5
2026-03-18
Dravet syndrome
-
2025-521858-42-00
5
2026-03-16
Hemophilia
-
2024-516476-15-00
9
2026-03-04
Advanced gastrointestinal stromal tumor (GIST)
-
2024-519622-20-00
1
2026-02-27
Advanced Solid Tumors Harboring RAS Mutation(S)