-
2023-508845-41-00
5
2025-03-11
Active juvenile idiopathic arthritis subtypes enthesitis-related arthr
-
2025-520777-39-00
6
2025-01-29
Complicated acute appendicitis
-
2024-511377-30-00
10
2025-01-23
SYMPTOMATIC OBSTRUCTIVE HYPERTROPHIC CARDIOMYOPATHY
-
2024-514656-32-00
4
2025-01-23
Suspected or confirmed Gram negative infections
-
2024-513420-41-00
10
2025-01-09
prematurity in neonates
-
2023-504713-76-00
5
2024-12-03
Dermatitis atopic
-
2024-512584-31-00
10
2024-11-11
Otoferlin gene-mediated hearing loss
-
2023-507178-41-00
9
2024-11-07
Hematologic Malignancies or Solid Tumors in Pediatric and Young Adults
-
2023-508760-29-00
5
2024-10-21
Chronic Rhinosinusitis With Nasal Polyps (CRSwNP)
-
2023-509618-12-00
5
2024-09-11
Crohn's Disease (CD)
-
2023-503859-10-00
5
2024-08-12
Moderate to Severe Plaque Psoriasis
-
2023-505043-39-00
5
2024-05-24
Duchenne Muscular Dystrophy
-
2022-503142-41-00
5
2024-05-06
Mucopolysaccharidosis type II
-
2022-500319-38-00
4
2024-05-03
Paroxysmal supraventricular tachycardia (PSVT)
-
2024-511342-40-00
7
2024-03-04
Congenital Hearing Loss Secondary to Biallelic Pathogenic Variants of
-
2023-504146-60-00
10
2024-02-07
lymphatic malformations associated with PIK3CA mutation
-
2022-500531-36-00
4
2024-02-02
Type 1 diabetes mellitus
-
2023-505000-27-01
4
2023-12-29
newly diagnosed pediatric FLT3-ITD positive and NPM1 wild-type AML
-
2022-502984-39-00
5
2023-12-13
Severe Uncontrolled Asthma
Asthma (an illness that causes breathing di
-
2022-502159-78-00
5
2023-12-06
Chronic Spontaneous Urticaria
-
2022-501997-20-00
7
2023-12-01
participants with isolated methylmalonic acidemia (MMA) due to
methylm
-
2022-501869-41-00
9
2023-11-14
Acute Lymphoblastic Leukemia, in Relapse
Lymphoblastic Lymphoma (Precu
-
2023-503906-35-00
9
2023-10-11
Severe or Moderate Hemophilia A with or without factor VIII inhibitors
-
2022-501899-26-00
5
2023-09-01
Asthma