-
2023-509809-76-00
5
2023-02-28
Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)
-
2024-514173-22-00
5
2023-02-28
Cystic Fibrosis
-
2023-503928-10-00
4
2023-02-01
Prodromal and Early Manifest Huntington’s Disease
-
2022-501744-15-00
5
2023-01-23
Obesity, Overweight
-
2024-511852-42-00
5
2023-01-19
Spinal Muscular Atrophy
-
2023-510061-10-00
3
2023-01-09
Clear cell renal cell carcinoma (ccRCC, first-, second- and third-line
-
2023-504867-18-00
5
2022-12-05
Patients with Paroxysmal Nocturnal Hemoglobinuria
-
2024-517881-40-00
4
2022-11-27
Antineutrophil cytoplasmic antibody (ANCA)- associated vasculitis (AAV
-
2023-505772-30-00
5
2022-11-09
Melanoma
-
2024-515637-14-00
5
2022-11-08
Cystic Fibrosis
-
2023-505866-27-00
5
2022-10-28
Chronic Lymphocytic Leukemia or Small Lymphocytic Lymphoma
-
2023-505579-53-00
5
2022-10-25
Diffuse large B-cell lymphoma (DLBCL)
-
2023-505992-54-00
3
2022-10-21
Advanced or Metastatic Non-small Cell Lung Cancer (NSCLC)
-
2023-506929-11-00
5
2022-10-17
Overweight and obesity
-
2023-503467-41-00
5
2022-10-12
Relapsed or Refractory Multiple Myeloma
-
2023-506871-88-00
3
2022-10-07
Relapsed/Refractory Multiple Myeloma
-
2023-509429-37-00
5
2022-10-03
Advanced or Metastatic Non-Small Cell Lung Cancer
-
2023-509750-58-00
5
2022-09-21
Polycythemia Vera
-
2023-504194-21-00
5
2022-09-13
PD-L1 Positive Metastatic Triple-Negative Breast Cancer
-
2023-504187-42-00
1
2022-09-12
Non-Hodgkin Lymphoma (NHL) and Chronic Lymphocytic Leukemia (CLL)
-
2023-506927-27-00
5
2022-08-29
Children with short stature either born small for gestational age or w
-
2023-509657-31-00
5
2022-08-24
Paroxysmal nocturnal haemoglobinuria (PNH)
-
2022-501380-40-00
4
2022-08-10
Diffuse large B-cell lymphoma (DLBCL)
-
2024-514891-41-00
6
2022-07-19
HR+, HER2- advanced or metastatic breast cancer