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2023-506927-27-00
5
2022-08-29
Children with short stature either born small for gestational age or w
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2024-511411-25-00
5
2022-08-25
X-Linked Retinitis Pigmentosa caused by mutations in the RPGR gene
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2023-507933-12-00
5
2022-08-18
Advanced or Metastatic Non-small Cell Lung Cancer (NSCLC)
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2024-514630-21-00
4
2022-08-11
HER2 positive (HER2+), Hormone Receptor positive (HR+) Early-stage Bre
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2024-516604-41-00
4
2022-08-08
Non-small Cell Lung Cancer
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2024-511068-10-00
5
2022-08-04
Sjögren’s Syndrome
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2023-509260-25-00
5
2022-07-12
Locally Recurrent Inoperable or Metastatic Triple-negative Breast Canc
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2023-509029-29-00
5
2022-06-29
Familial Chylomicronemia Syndrome (FCS)
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2022-500014-26-00
5
2022-06-24
Locally-Advanced unresectable or Metastatic breast cancer (MBC)
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2024-512378-91-00
4
2022-06-24
Unresectable or Advanced Melanoma
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2023-509345-12-00
5
2022-06-22
Multiple Sclerosis
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2023-505764-11-00
4
2022-06-10
Pruritus associated with Primary Sclerosing Cholangitis (PSC)
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2024-516157-41-00
4
2022-05-27
Metastatic pulmonary large-cell neuroendocrine carcinoma (LCNEC)
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2023-509943-28-00
5
2022-05-18
Stage IA2-IA3 non-small cell lung carcinoma, with EGFR mutation type (
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2023-507069-25-00
4
2022-04-29
Amyloid Light Chain Amyloidosis
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2024-516914-39-00
5
2022-04-27
Metastatic or unresectable melanoma
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2023-510054-16-00
4
2022-04-26
Primary Sjogren's syndrome
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2024-513147-90-00
5
2022-04-26
Primary Immune Thrombocytopenia
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2023-505747-40-00
6
2022-04-20
Severe or Moderate Hemophilia A
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2024-512745-16-00
5
2022-04-13
Non–Transfusion-Dependent Alpha- or Beta-Thalassemia
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2023-503517-30-00
5
2022-04-01
Extensive-stage small-cell lung cancer
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2023-506361-56-00
5
2022-04-01
Endometrial cancer
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2024-511901-52-00
4
2022-03-24
Adult patients affected by recurrent/metastatic, platinum resistant na
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2024-511633-35-00
4
2022-03-21
Mantle cell lymphoma