-
2022-500535-36-00
5
Moderately to severely active ulcerative colitis
-
2022-500537-84-00
5
Moderately to severely active ulcerative colitis
-
2023-505030-99-00
1
Post-Traumatic Stress Disorder (PTSD)
-
2023-505311-20-00
5
Metastatic Non-Small Cell Lung Cancer
-
2024-516253-49-00
4
advanced/metastatic HER2-positive breast carcinoma
-
2023-508062-15-00
5
Primary Hyperoxaluria (PH) of all subtypes (PH1, PH2 and PH3)
-
2024-511296-15-00
5
Musculoskeletal diseases
-
2024-513724-42-00
10
Medulloblastoma
-
2024-513889-19-00
5
Multiple Myeloma
-
2024-514246-37-00
4
Idiopathic pulmonary fibrosis (IPF)
-
2024-517133-40-00
5
newly diagnosed, non-metastatic, SHH-activated, TP53-wt, non-MYC ampli
-
2024-518349-85-01
5
small bowel adenocarcinoma
-
2024-519504-27-00
5
Relapsed Refractory Multiple Myeloma
-
2024-519638-22-00
5
IgA nephropathy
-
2025-520554-11-00
5
Cardiovascular Disease
-
2025-521037-86-00
5
Immune system diseases
-
2025-521113-13-00
10
Early Parkinson’s Disease
-
2025-521221-32-00
5
Advanced or Metastatic Non-Small Cell Lung Cancer
-
2025-521981-90-00
1
Advanced Solid Tumors
-
2025-522167-15-00
5
Ovarian Cancer Platinum-Sensitive Ovarian Cancer (PSOC)
-
2025-522373-10-00
5
Progressive pulmonary fibrosis and Idiopathic pulmonary fibrosis
-
2025-522586-30-00
5
Psoriatic Arthritis
-
2025-522818-23-00
5
Small Cell Lung Cancer (SCLC)
-
2025-523087-20-00
5
Duchenne muscular dystrophy